Archives: Agenda

• Challenges and limitations of rare disease research: how new solutions can help to overcome this
• Embracing a patient centric approach in rare disease trials through digital health
• Opportunities for innovation for orphan drug trials in the US

• Learn about a new comprehensive approach to assessing RBQM adoption
• See recent data on current and future levels of RBQM adoption among industry sponsors and CROs
• Discuss a maturity model that characterizes levels of adoption among industry sponsors
• Discuss perceived challenges associated with the implementation of RBQM components
• Discuss opportunities and benefits of RBQM implementation

• Sponsors’ roles in supporting sites in order to increase trial efficiency and decrease overall timelines
• Where can clinical trial sponsors better support patients with rare diseases both during trials and in the long term?
• Lessons learned from Moderna’s experience of site and patient engagement during clinical trials

• How sponsors can support and reduce burden on sites in order to shorten overall trial timelines
• Top tips for training site staff with new processes and technology
• Managing relationships with short staffed and under resourced sites to ensure your trial stays on track

Visit our exhibitors’ booths throughout the day and collect stamps in order to enter our Prize Draw and be in for a chance of winning Apple devices or Amazon vouchers. The Prize Draw will take place in the Exhibition Hall, make sure you don’t miss out!

• Navigating new regulations around clinical trials smoothly and successfully
• The impact of artificial intelligence: how far can we expect to move forward in the next 12 months?
• Patient centricity in clinical trials: how can burden be reduced in order to make trials easier for patients to participate in?
• How may geopolitical and geoeconomic events including the financial crisis, the Inflation Reduction Act and the upcoming election impact clinical trials in the US?
• Technological developments into 2025 and beyond: what changes can we expect to see in the next 3-5 years?

MODERATOR: Revati Tatake, Global Head of Pharma Research, Analysis and Competitive Intelligence, GlobalData Healthcare

A look at the pros and cons of various outsourcing models including Full-Service Outsourcing (FSO), Functional Service Provision (FSP), and single service. A discussion of the benefits of a hybrid approach are explored.

• Insights on the differences between represented and underrepresents populations on their barriers to care
• Challenges and nuances of rare disease patients’ journey to receive a diagnosis
• Mental health and well-being: the emotional toll rare diseases take on patients and caregivers
• Exploring overall experiences individuals have had within the healthcare system: strengths and areas for improvement

• Overview of evolving challenges and solutions in clinical supply chain procurement
• Examination of the impact of the geopolitical and geoeconomic climate on procurement
• Regulatory considerations and compliance challenges in clinical supply chain management