Clinical Trials in Rare Diseases - Virtual Event

Patient Advocate

Executive Director, Patient Advocacy
AGTC

Chief Executive Officer
Akan Biosciences

Senior Director, Health Economics and Outcomes Research EMEAC
Alexion Pharmaceuticals

Vice President, Patient Experience/STAR & Patient Experience and Advocacy
Alexion Pharmaceuticals

Chief Science Officer
Coronis Neuroscience

Director, Clinical Development
Dicerna Pharmaceuticals

MD MBA, Director, The Weinberg Child Development Center and Keshet Center for Autism
Safra Children's Hospital at Sheba, and Tel Aviv University, Israel

Founder and Chairman
Partners For Patients, PfP.NGO

PhD, Clinical Advisor Consultant
Mereo BioPharma Group

Founder and Chief Operating Officer
Oncoheroes Biosciences

Senior Vice President, Center for Rare Diseases
PRA Health Sciences

Director, Clinical Patient Advocacy
PTC Therapeutics

Translational Medicine Leader
Roche

Country Medical Director, UK and Ireland
Sarepta Therapeutics

Clinical Project Leader & Portfolio Lead, Rare Genetic Diseases and Rare Blood Disorders
Sanofi Genzyme

Assistant Professor
Tel Aviv University

Senior Director, Clinical Affairs
Zogenix, Inc.

Sr. Clinical Trial Manager, Associate Director Clinical Operations
Medpace

International Head of Clinical Client Services - Life Sciences
Volt International

Associate Director of Product Innovation
Axiom Real-Time Metrics

Founder & CEO
Axiom Real-Time Metrics